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NDF Board & Staff

Dr. Carmen Bertoni

Dr. Bertoni is an expert on the field of neuromuscular disorders and, in particular, gene therapy. She is a former Associate Professor in the Department of Neurology at UCLA. She received her BS from the University of Perugia, Italy and earned her Ph.D. from the same university after completing her graduate program at Tulane as an exchange student. During her postdoctoral fellowship at Stanford she developed non-viral mediated gene therapies for muscular dystrophies pioneering gene correction strategies using oligonucleotides. While at UCLA she developed several novel approaches to the treatment of neuromuscular diseases. She has discovered and patented new molecules for the treatment of certain types of neuromuscular diseases along with other genetic disorders. She currently serves as a consultant for pharmaceutical companies and venture capital firms.